Partnering with Clinicians and Researchers to Advance Precision Therapies
Our Commitment to the Medical Community
At Dawn Therapeutics, we believe that medical professionals are essential partners in our mission to deliver next-generation treatments for rare and complex diseases. We work closely with:
- Physicians and specialists in neurology, genetics, orthopaedics, and metabolic medicine.
- Clinical trial investigators and research coordinators.
- Genetic counsellors and diagnostic laboratories.
- Patient advocacy and support networks.
Clinical Resources
We provide healthcare professionals with:
Disease Education Materials
Updated information on the epidemiology, pathophysiology, and genetic basis of targeted diseases
Treatment Mechanism Overviews
Easy-to-understand summaries of how our therapies work at the molecular level.
Diagnostic Guidelines
Tools to aid early identification and referral
Continuing Medical Education (CME)
Access to scientific webinars and accredited learning sessions.
Clinical Trials
Dawn Therapeutics is actively conducting and planning clinical trials in:
Lysosomal storage disorders
- MPS I
- II
- III
- IV
- VI
- VII
- IX
CNS disorders
- Alzheimer’s
- Parkinson’s
- Huntington’s
- Autism Spectrum Disorder
- Addiction Disorders
Musculoskeletal disorders
- Osteoarthritis
- Duchenne Muscular Dystrophy
- Friedreich’s Ataxia
- ALS
We invite:
- Referrals for trial eligibility screening.
- Sites to apply for participation in upcoming studies.
- Investigators to collaborate in protocol development.
Review eligibility criteria for the relevant trial.
Submit patient details securely via our referral portal.
Our clinical team will confirm eligibility and coordinate with your practice.
Medical Affairs Team
Our Medical Affairs team provides:
Rapid response to clinical queries.
Access to scientific data and safety information.
Collaboration on publications and congress presentations.
Collaboration Opportunities
Investigator-Initiated Trials (IITs)
Submit proposals for Dawn-supported research.
Biomarker Development Projects
Work with our R&D team on validation studies.
Registry & Natural History Studies
Contribute data to accelerate research in rare diseases.