Molecular science
Gene and RNA research, nucleic acid chemistry and delivery design.
About us
Scientists, clinicians and collaborators united by a shared ambition: helping genetic medicines reach the tissues that need them.
Explore about us01 / The beginning

Founded in the UK · 2019
Dawn brings together scientists, clinicians and entrepreneurs to tackle a central challenge in genetic medicine: getting therapeutic instructions to the tissues that need them.
Our lead focus is Hurler syndrome. Our broader ambition is to build delivery technologies that support new approaches to rare genetic, neurological and musculoskeletal diseases.
The disease behind our lead programme02 / Connected expertise
Gene and RNA research, nucleic acid chemistry and delivery design.
Experience of disease, patient needs and translational research.
Manufacturing, safety studies and regulatory planning.
03 / Our delivery approach

sLV
A modified viral carrier designed to deliver a functional gene in vivo.
Explore the science
iLNP
Lipid-based carriers engineered for tissue targeting and flexible genetic payloads.
Explore the science04 / How we work
We use milestone-based work packages and formal Go/No-Go decision points to keep development focused, measurable, and capital efficient.
05 / A focused path forward
Generate and examine preclinical evidence for DAWN-01.
Develop manufacturing, dose strategy and safety workstreams.
Align the evidence package and regulatory plan before clinical development.
06 / The people behind Dawn

Founder & Chief Executive Officer
A career connecting surgery, scientific research and therapeutic innovation informs Dawn’s approach to translating new ideas into development programmes.
Meet the scientific teamBuild a partnership with DawnClear answers
Dawn Therapeutics is a UK preclinical biotechnology company developing delivery platforms for genetic medicines. Its lead programme is DAWN-01 for Hurler syndrome.
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